ALS RESEARCH

A major part of our current work began in 2007 with the launch of the Pre-Symptomatic Familial ALS (Pre-fALS) study. Pre-fALS was motivated, in large part, by our belief that successful treatment of a neurodegenerative disease such as ALS would require early, and perhaps even pre-symptomatic, intervention. Our focus on the familial/genetic form of ALS was out of necessity: Individuals who carry an ALS-causing gene mutation are the only group known to be at an elevated risk (compared to the general population) for developing ALS - and therefore the only group in whom the study of pre-symptomatic ALS is feasible. Critical to studying the earliest stages of ALS and to advancing our goal of preventing ALS, has been the development of biomarkers of pre-symptomatic disease, an area in which we have been leaders in the field... Our research program focuses on advancing ALS therapy development by identifying and filling knowledge gaps that have, in the past, hampered the development of..

Also known as: ALS, ALS Research Collaboration, ALS Research Collaboration at University of Miami

Primary location: Miami United States