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1-16 of 16 results

  • www.hse.ie
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The National Rare Diseases Office (NRDO) was established by the HSE in 2015. We are the national rare disease ‘coordination hub' and the HSE main contact and driver of rare disease initiatives and projects. In accordance with the National Rare..
Relevance: 77.59239
  • rare-diseases.ca
  • 23
Our Emerging Team in Rare Diseases aims to undertake collaborative translational research with the objective of helping to inform the development of drug coverage decision-making models relating to government funding of drug therapy for rare..
Relevance: 76.25076
  • www.recordatirarediseases.com
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Recordati Rare Diseases Inc. (RRD) is a biopharmaceutical company committed to providing therapies to the underserved and often overlooked rare disease communities of the United States. Recordati Rare Diseases is part of the rare diseases business..
Relevance: 63.000122
  • www.rrd-rsvp.com
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Relevance: 61.353638
Relevance: 36.00374
  • www.hra-pharma-rare-diseases.com
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HRA Pharma Rare Diseases - At HRA Pharma Rare Diseases, we are a team of passionate people, dedicated to rare and ultra-rare diseases such as Cushing's syndrome and Adrenocortical Carcinoma and providing important medicines: Metopirone (Metyrapone),..
Relevance: 35.45824
Relevance: 35.033974
Relevance: 31.925564
  • www.rareneuro.com
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Most individuals with a rare disease have never met a specialist in their disorder, and care is inconsistent. Quality of life is often extremely poor, and over 1/3 of deaths in early childhood are due to a rare disease. At the Center for Rare..
Relevance: 31.370258
Relevance: 31.016697
Relevance: 31.016697
  • orphandrugsus.com
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Incorporating Diversity in Clinical Trials: Uncover the untapped potential of incorporating people with blindness and disabilities within clinical trial design teams. Learn how their unique insights and experiences bring invaluable depth to the..
Relevance: 28.677263
  • www.carbaglu.com
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CARBAGLU has well-established support programs help educate your patients and caregivers and to provide financial assistance to eligible patients, including a $0 copay.**... The medication helps to replace the cofactor NAG that your body cannot..
Relevance: 24.250406
  • rarediseasesday.wustl.edu
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According to the National Institutes of Health (NIH), a disease is rare if it affects less than 200,000 people in the United States. Over 25 million Americans live with a rare disease-and nearly half of these patients are children. For the over 7,000..
Relevance: 24.173252
  • thinkporphyria.org
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Recordati Rare Diseases is a pharmaceutical company that provides treatment for patients with rare diseases. Created in 1990, Recordati Rare Diseases is one of the most active companies in the field of rare diseases... Think Porphyria provides..
Relevance: 22.844975
  • chiesirarediseases.com
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Chiesi is the largest global pharmaceutical group to be awarded B Corp Certification, a recognition..... Chiesi Global Rare Diseases is a family-owned and run biopharmaceutical company with a commitment to providing transformative care to patients..
Relevance: 12.867716