Companies similar to ACTION DUCHENNE
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91-120 of 4,819,939 results

  • www.triaxiahealth.com
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At TriAxia Health, our mission is to improve health outcomes for patients living with rare diseases by enabling the selection and discovery of the most effective treatments for each patient. We do so through collaboration across leading provider..
Relevance: 17.601347
  • www.abxis.com
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ISU ABXIS is a biotechnology company dedicated to the development of new and novel bio-therapeutics that will enhance the lives and ease the suffering of patients struggling with cancer and rare diseases... ISU ABXIS is focused on the development of..
Relevance: 17.56452
  • www.washingtonnationalsopeningday.com
The unofficial first day of summer 2024 is almost here, and Washington Nationals Opening Day tickets are on sale now! CJ Abrams, Joey Meneses, and the boys are ready to make this season something special, and there's no better way to kick off the..
Relevance: 17.564352
  • www.stampoutoncho.org
Onchocerciasis (river blindness) elimination is at risk of losing momentum now that the disease is under control as "a public health problem." In most endemic areas, blindness is increasingly rare and skin disease is not as prevalent as it once was..
Relevance: 17.547132
  • eu.aledotimesrecord.com
Get the latest breaking news, sports, entertainment and obituaries in Aledo, IL from Aledo Times Record... Illinois is home to a rare total solar eclipse on April 8, 2024. We have important info about how to watch the eclipse and eclipse times...
Relevance: 17.53974
  • www.biozentrum.unibas.ch
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Congenital muscular dystrophy is a rare hereditary disease which leads to muscle weakness and loss already at young age. The more than thirty known forms of this neuromuscular disease differ in the type of genetic defect and in the severity of..
Relevance: 17.449986
  • www.rarebase.org
Rarebase is a public benefit precision medicine company that leverages cutting-edge technology and biology to discover and develop treatments for the millions of people worldwide living with a rare disease... Rarebase is already developing its first..
Relevance: 17.412258
  • creatineinfo.org
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The Association for Creatine Deficiencies (ACD) was established in 2012, by parents of children diagnosed with a Cerebral Creatine Deficiency Syndrome (CCDS) that decided a rare disease needs a unified community to affect change for the future. The..
Relevance: 17.394423
  • patientwarrior52.com
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Our Patient Warrior is our son Dante who was diagnosed with a very rare neuro degenerative disorder in 2017. He has spastic paraplegia type 52 or SPG52. We're here to share Dante's story, raise awareness of this rare disease, connect with other AP-4..
Relevance: 17.389097
  • www.biomarin.com
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Founded 25 years ago, BioMarin is a global biotechnology company dedicated to transforming lives through genetic discovery... BioMarin is a world leader in developing and commercializing innovative biopharmaceuticals for rare diseases driven by..
Relevance: 17.347315
  • www.lamlab.org
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We are a multi-disciplinary center focusing on the care of patients with LAM and other rare lung diseases. In addition to the care of patients with LAM, we conduct both clinical and basic science research focusing on this disease... LAM Lab focuses..
Relevance: 17.29156
  • impulsate.org
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IMPULSAT is the official spanish non-profit association representing people having Congenital Merosin-deficient Muscular Dystrophy (LAMA2-CMD1A). It is a rare disease that affects 1 in 100.0000 people with unknown cure... We are a non-profit..
Relevance: 17.273132
  • reflectionbio.com
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Currently, there is no approved treatment for BCD. ReflectionBio® is developing gene therapy for BCD. BCD gene therapy has shown promising results in preclinical study. We are advancing BCD gene therapy R&D into human clinical trial.....
Relevance: 17.231092
  • www.rdh12sight.org
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The RDH12 Fund For Sight is the only non-profit foundation dedicated to the cure of this rare eye disease. Donate Today!..
Relevance: 17.220829
  • pallavshah.co.uk
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We diagnose & treat all aspects of lung disease with a particular interest in Bronchoscopy, Lung Cancer, COPD, & Asthma. We are experienced in managing complex and rare conditions...
Relevance: 17.213242
  • treatablefoundation.org
CABs were created in the 90s for HIV/AIDS, hepatitis and breast cancer. Some rare disease European federations, with or without EURORDIS support, have already gained experience with CAB-like initiatives...
Relevance: 17.201412
  • stonypointlifesciences.com
Stony Point Life Sciences Consulting, LLC focuses on drug development from Discovery through late-stage Clinical Development. We have proven success with US/global regulatory approvals across a wide range of therapeutic disciplines in Infectious..
Relevance: 17.173674
  • www.genius-chd.com
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Identification of key biomarkers for predicting CAD progression in inflammatory bowel disease via machine-learning and bioinformatics strategies March 7, 2024..
Relevance: 17.134384
  • www.rtrtechnovation.com
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Our mission is to develop novel technologies that diagnose and treat chronic disease states. We do this by researching rare cases of disease remission and ultimately mimicking those responses. To achieve this, our first product, Mivatana TM, is a..
Relevance: 17.133568
  • www.ashibio.com
āshi bio is developing novel therapies for patients with rare bone and connective tissue disorders that have the potential to prevent the onset of symptoms or slow the progression of disease...
Relevance: 17.106964
  • cyclepharma.com
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Cycle Pharmaceuticals is a global, privately-owned and patient-dedicated biotechnology company headquartered in Cambridge in the UK. Our mission is to utilise the latest pharmaceutical technologies to deliver superior drug treatments to better serve..
Relevance: 17.01851
  • www.oraxiontx.com
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At Oraxion, we are developing a class of polymer drugs that target diseases where aberrant cholesterol and lipid accumulation is implicated as one of the key causes. We are advancing a diverse pipeline covering a broad range of rare diseases with our..
Relevance: 17.007725
  • www.advanzpharma.com
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ADVANZ PHARMA is a global pharmaceutical company with a strategic focus on specialty and hospital pharmaceuticals. We are committed to improving patients' lives by providing and enhancing the specialty, hospital, and rare disease medicines they..
Relevance: 16.986261
  • panrare.com
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PanRARE CoE is located in Hong Kong, Asia's central city. The Center's mission is to help both paediatric and adult patients who suffer from rare diseases. For example, in the neuromuscular disorders area, the PanRARE CoE provides expert opinion and..
Relevance: 16.968153
  • ceriumpharma.com
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Cerium Pharmaceuticals is dedicated to creating efficacious therapies for patients with kidney diseases. Cerium is currently focused on developing the first drug approved for a very rare kidney disease called Primary Membranous Nephropathy (PMN)...
Relevance: 16.949791
  • www.aceragen.com
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Aceragen is a rare disease biopharmaceutical company. We address rare, orphan diseases that typically have no available treatment, and strive to develop novel therapies which can have a positive impact on the lives of patients and families. As such,..
Relevance: 16.941319
  • rebornabiosciences.com
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Reborna Biosciences, Inc. was established in 2018 as a biotech start-up to create drugs to meet high unmet medical needs such as drugs for the treatment of rare genetic diseases. There are said to be 9,000 or more rare diseases today, of which many..
Relevance: 16.917389
  • www.eradtx.com
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With an initial focus on Tay-Sachs Disease, we create novel biological agents to treat mis-folded protein diseases (ERAD diseases).... Welcome to ERAD Therapeutics Inc. (ERAD). The Company was formed to develop therapeutics for the treatment of Rare..
Relevance: 16.8883
  • www.clevelandcountywater.com
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Cleveland County Water will be closed on Monday, May 27, 2024 for the Memorial Day Holiday. The office will reopen on Tuesday, May 28, 2024 at 8:00 a.m...
Relevance: 16.875849
  • www.thelevimilesfoundation.org
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The Levi Miles Foundation was founded for the purpose of providing support and resources to children with disabilities and rare diseases, as well as, to promote acceptance and inclusion of all individuals within our communities. Our vision and..
Relevance: 16.86498