Companies similar to REGENXBIO
Sign up to Download

1-30 of 6,028,302 results

  • genebiotherapeutics.com
  • 1
  • 1
  • 4
Gene Biotherapeutics is a publicly-traded, clinical development-stage biotechnology company engaged in the clinical advancement and commercialization of DNA-based biotherapeutics, primarily for the treatment of cardiovascular disease... We are a..
Relevance: 44.739075
  • www.askbio.com
  • 6
  • 3
  • 15
AskBio is a leading, clinical-stage gene therapy company dedicated to developing AAV gene therapies for genetic and complex disorders. Learn more about our gene therapy technology and current clinical trials... AskBio is headquartered in Research..
Relevance: 37.564735
  • www.vivet-therapeutics.com
  • 1
  • 12
Vivet is building a diversified gene therapy pipeline based on novel recombinant adeno-associated virus (rAAV) technologies developed through its partnerships with, and exclusive licenses from, the Fundación para la Investigación Médica Aplicada..
Relevance: 37.37748
  • www.regenxbio.com
  • 1
  • 2
  • 17
REGENXBIO is a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy... Our gene therapy product candidates are designed to deliver genes to cells to address genetic defects or to enable..
Relevance: 36.950893
  • exumabio.com
  • 1
  • 4
  • 13
EXUMA Biotech is a clinical-stage biotechnology company discovering and developing cell and gene therapies for solid & liquid tumors... As part of our commitment to make cell therapies more accessible to earlier lines of therapy, we are developing..
Relevance: 35.330185
  • www.orphina.com
  • 1
  • 2
Orphina is a biotechnology company at seed stage, focused on preserving and prolonging muscle health. Our initial clinical gene therapy program is for a rare disease indication of unmet medical need. Our technology allows re-dosing while limiting..
Relevance: 34.45769
  • www.genecure.com
  • 1
  • 1
GeneCure Biotechnologies is an emerging biotechnology company focused on developing its patented gene transfer technology into effective treatments for various genetic diseases, infectious diseases, and cancers... GeneCure's platform technology is..
Relevance: 34.251625
  • exegenesisbio.com
  • 3
  • 7
Exegenesis Bio is a clinical-stage global cell and gene therapy company that operates in Philadelphia, Boston, China, and Singapore. Founded in 2019 with strong financial backing, the company has built a broad pipeline of innovative genetic medicines..
Relevance: 33.532322
  • interiusbio.com
  • 1
  • 1
  • 15
Interius BioTherapeutics is an early-stage biotechnology company expanding the potential of cell and gene therapy by developing next generation delivery technology based on inventions from the laboratory of Dr. Saar Gill at the University of..
Relevance: 32.83272
  • www.abeonatherapeutics.com
  • 2
  • 1
  • 19
Abeona Therapeutics Inc. is a clinical-stage biopharmaceutical company developing cell and gene therapies for serious diseases. Abeona's lead clinical program is EB-101, its investigational autologous, gene-corrected cell therapy for recessive..
Relevance: 32.795383
  • www.expressiontherapeutics.com
  • 3
  • 1
  • 8
Expression Therapeutics, Inc. is a fully integrated clinical stage gene and cell therapy company developing novel, potentially curative, therapeutics for deadly childhood and adult genetic diseases... The Company's scientific breakthrough in..
Relevance: 32.583664
  • poseida.com
  • 5
  • 2
  • 33
Poseida Therapeutics is a clinical-stage biopharmaceutical company advancing differentiated cell and gene therapies with the capacity to cure certain cancers and rare diseases. The Company's pipeline includes allogeneic CAR-T cell therapy product..
Relevance: 32.42891
  • www.scian.com
  • 1
  • 2
  • 2
SCiAN Services is a Contract Research Organization (CRO) providing integrated clinical trial services and data systems. With 30+ years of experience in IND stage clinical trials and 700 studies completed, SCiAN's therapeutic area expertise includes..
Relevance: 30.641624
  • sparingvision.com
  • 3
  • 2
  • 29
Our goal is to harness the potential of gene therapy and genome editing to bring cutting-edge innovation into ocular disease drug discovery and development... SparingVision's lead product, SPVN06, is a breakthrough gene therapy approach targeting..
Relevance: 30.579903
  • toxplusmonitoring.com
  • 1
  • 1
  • 2
Tox Plus Monitoring is a dedicated, client-focused company that caters to global nonclinical study monitoring services. We focus on pre-clinical study monitoring, toxicology, pharmacology, and gene therapy. We serve the biopharmaceutical and..
Relevance: 30.497013
  • reflectionbio.com
  • 1
  • 1
Currently, there is no approved treatment for BCD. ReflectionBio® is developing gene therapy for BCD. BCD gene therapy has shown promising results in preclinical study. We are advancing BCD gene therapy R&D into human clinical trial.....
Relevance: 30.495033
  • strm.bio
  • 2
  • 1
  • 15
Based in Boston, MA, STRM.BIO is a pre-clinical, VC-backed biotechnology company that is leveraging extracellular vesicles (EVs) to deliver gene therapy in a better way: simpler, safer, practical... We are assembling a team that shares our values..
Relevance: 30.415123
  • www.appliedstemcell.com
  • 2
  • 4
  • 16
As a leading cell and gene therapy CRO/CDMO, Applied StemCell is a proud supporter of gene editing and stem cell therapy development. With two high-impact platforms, CRISPR/TARGATT™ Genome Editing and iPSC (GMP grade), we seek to help advance the..
Relevance: 30.237791
  • www.gene-factory.com
  • 1
  • 1
cancer research, genetic constructs for cancer gene therapy, translational control, gene expression enhancement, recombinant protein biotechnology, forensic and medical diagnostics, biochemistry of polyphenols (anthocyanins, resveratrol) in cancer..
Relevance: 30.19013
  • www.chancepharmaceuticals.com
  • 1
  • 4
Chance Pharmaceuticals is a clinical-stage biotechnology company focusing on discovering, developing... Founded in 2015 by a team of passionate and experienced experts in inhalation therapy, our vision is to..
Relevance: 30.13674
  • vigeneron.com
  • 1
  • 2
  • 6
ViGeneron was founded in 2017 as a spin-off of the Ludwig-Maximilians-University (LMU) Munich. The company's founding team includes highly experienced executives and internationally renowned experts with track records in developing retinal gene..
Relevance: 30.02711
  • www.lnsbioscience.com
  • 1
As your innovation Partner in Genetic Diagnostics and Gene Therapy. LNS Bioscience Corp. is a leading biotechnology company focusing on genetic diagnostics and gene therapy... We are staying in cutting edge technology and can provide most advanced..
Relevance: 29.79969
  • silvercreekpharma.com
  • 4
  • 2
  • 16
Silver Creek is a clinical stage biotechnology company. Scp776 is under active clinical development for the treatment of stroke. We are applying Smart Growth Factor™ technology to treat additional CNS diseases... Silver Creek has developed a first-..
Relevance: 29.678167
  • www.swanbiotx.com
  • 4
  • 1
  • 11
SwanBio Therapeutics is a clinical-stage gene therapy company that aims to bring life-changing treatments to people with devastating and inherited neurological conditions... At SwanBio Therapeutics, our goal is to prevent the progression of..
Relevance: 29.594118
  • www.genebiotec.org
  • 1
  • 2
Gene Biotec (cell processing & Research Institute) is a service provider for clinical researcher, Medical Oncologist, Haematologist and regulatory experts involved in cell processing and stem cell therapy. We endeavour to promote our diversity, so..
Relevance: 29.480562
  • www.eg427.com
  • 1
EG 427 is a French biotechnology company that pioneers a new approach in gene therapy called pinpoint gene therapy... Based in Paris, EG 427 was founded by a world-renowned team in the field of HSV-1 vectorology and spinal cord injury-related..
Relevance: 29.290129
  • www.immutep.com
  • 6
  • 6
  • 20
Immutep is a clinical-stage biotechnology company at the forefront of developing novel LAG-3 Immunotherapy for cancer and autoimmune diseases. We are pioneers in the understanding and advancement of therapeutics related to Lymphocyte Activation..
Relevance: 29.25452
  • omegatherapeutics.com
  • 3
  • 2
  • 16
Omega Therapeutics is a clinical-stage biotechnology company pioneering the development of a new class of programmable epigenomic mRNA medicines for unprecedented control of gene regulation and cellular function. Through our OMEGA platform, we..
Relevance: 29.226068
  • ingeneron.com
  • 2
  • 2
  • 11
InGeneron is a clinical-stage biotechnology company developing cell-based therapies to redefine the standard of care in orthopedics... At InGeneron we use the term "regenerative cell therapy" since there are many different cell types and..
Relevance: 28.852154
  • www.ewingcole.com
  • 126
  • 10
  • 121
REGENXBIO is a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy based on its proprietary NAV® Technology... Thomas Jefferson National Accelerator Facility is a U.S. Department of..
Relevance: 28.64941