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  • www.duchenneuk.org
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Duchenne UK is collaborating on an initiative to improve DMD care throughout the UK by providing clinical recommendations... Duchenne UK is not only funding treatments for earlier stages of DMD but investing in improving quality of life for..
Relevance: 35.30262
  • www.duchenneandyou.com
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Duchenne and You is a resource dedicated the people who's lives have been touched by Duchenne muscular dystrophy (DMD)... We are here to help guide you through the available information on DMD so you or your loved one can focus on living the best..
Relevance: 34.142227
  • www.northstardmd.com
The North Star Project was set up in 2003 to help drive improvements in services and set national standards of care for children living with Duchenne Muscular Dystrophy (DMD). The overall aim is to optimise the care of young patients with Duchenne..
Relevance: 32.240627
  • dmdcare.guide
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Duchenne muscular dystrophy (DMD or Duchenne) is a difficult, complex diagnosis to understand and manage. This is not a world that anyone enters willingly. The Muscular Dystrophy Association, Parent Project Muscular Dystrophy (PPMD), TREAT-NMD and..
Relevance: 30.313742
  • dfsg.org.uk
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The DFSG is a UK national charity, run by families for families affected by DMD. We have been bringing people together for mutual support, information sharing and social activities since 1987... Families Supporting Families You are not alone...
Relevance: 30.292475
  • www.duchennedatafoundation.org
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DDF provides training to all stakeholders. Our goal is to empower the global dystrophinopathy community voice to ensure research is patient and family centred and led... We bring together fragmented data pieces of the Duchenne and Becker muscular..
Relevance: 29.442307
  • vision-dmd.info
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Vamorolone is an innovative steroid-like drug designed to retain or improve corticosteroid efficacy and increase membrane stabilization with the potential for reduced side effects. Preclinical studies suggest that vamorolone has the potential to..
Relevance: 26.531452
  • www.seanandkem.com
Sean and Kem have nothing in common...apart from being the best friends in the world. Sean is an out-going, silly, 24-year-old from the north side of Dublin. He has (DMD) Duchenne Muscular Dystrophy. He is confined to a wheelchair and finds it..
Relevance: 24.902624
  • www.prohostbiotech.com
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Italfarmaco in the NEWS From Milan, Italy: Today, Italfarmaco announced that the U.S. Food and Drug Administration (FDA) has approved Duvyzat™ (givinostat) - a novel histone deacetylase (HDAC) inhibitor, for the treatment of patients 6 years or older..
Relevance: 24.414814
  • www.myogenebio.com
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Our lead program is a gene editing therapy, MyoDys 45-55, for Duchenne muscular dystrophy (DMD), a devastating muscle wasting disease. MyoGene Bio utilizes new technologies to have a strong positive effect on disease progression by targeting the..
Relevance: 24.019827
  • www.consortium.ai
At Consortium.AI, we are developing bioavailable small chemical compounds with exon-skipping function. We aim to target both the underlying genetic mutations as well as the secondary complications, alone or in combination with other treatments, with..
Relevance: 23.45354
  • duchennetherapynetwork.com
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The mission of DTN: Duchenne Therapy Network is committed to address the under-represented needs of the Duchenne Muscular Dystrophy community... Duchenne Therapy Network was created to help those who have been diagnosed with Duchenne Muscular..
Relevance: 22.83042
  • hamillhomecare.co.uk
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At Hamill Homecare, we make care personal. We believe in doing things differently and believe that complex care doesn't have to be complex. We have years of experience in helping to manage chronic illness and provide quality home care for those..
Relevance: 22.039152
  • www.rally4rj.org
We believe RJ is going to make a difference in people's lives and we want to make a difference in his life. RJ deserves an opportunity to achieve all his dreams!... Our mission as a family is to promote awareness of Duchenne Muscular Dystrophy among..
Relevance: 21.911633
  • mdxlifesciences.com
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MDX LIFESCIENCES, Inc. is a clinical stage biotechnology company developing autologous transplantation for tissue and organ regeneration... Our development programs are primarily focused Myocardial Ischemia, reperfusion injury and neurodegenerative..
Relevance: 21.733355
  • www.capricor.com
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Capricor Therapeutics is a publicly traded (NASDAQ: CAPR) biotechnology company with a mission to develop groundbreaking therapies that make a meaningful impact on patients' lives. Capricor is focused on the development of biologics, primarily cell..
Relevance: 21.522678
  • www.creatingcosmo.com
Please enjoy and share the images taken at past Cure Duchenne events… 2012 - Champions to Cure Duchenne Photos..
Relevance: 21.440971
  • defeatduchenne.ca
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Defeat Duchenne Canada is the country's only national charity dedicated to ending Duchenne muscular dystrophy. Our goal is to provide leadership in research, advocacy and support to ensure our boys and young men can live long and active lives.....
Relevance: 21.387209
  • www.fibrogen.com
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We work at the intersection of groundbreaking science and patient need. Our research and development teams seek to identify and develop innovative drugs with the greatest promise of becoming first-in-class medicines for the treatment of chronic and..
Relevance: 21.191072
  • www.duchenne.org.uk
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We aim to stop Duchenne muscular dystrophy being a death sentence for hundreds of thousands of boys worldwide... We are helping turn the hope of treatments into reality. Critical treatments are in clinical trial thanks to our funds... We focus on..
Relevance: 20.416656
  • www.dmdtrust.com
If you're reading this page then you have more than a passing interest in common with us..... Duchenne Muscular Dystrophy Trust - committed to funding and furthering research through effective giving - to help deliver a cure for Duchenne Becker..
Relevance: 20.227224
  • www.actionduchenne.org
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While we hope that research and clinical trials will one day lead to a treatment, or cure, for Duchenne, we believe it is vital to support families living with the condition today. We support families from diagnosis through their whole Duchenne..
Relevance: 20.140585
  • www.duchennetracker.com
Duchenne Tracker, a web that will help you establish your patient's dosage regimen...
Relevance: 19.633791
  • www.cdmd.ucla.edu
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Our mission is to build a supportive community to help us end Duchenne Muscular Dystrophy by raising money for ground-breaking research, spreading awareness, and providing aid to children and families with Duchenne... A program of PPMD which serves..
Relevance: 19.477179
  • www.duchenneemergency.co.uk
Duchenne A and E pack is to enable A and E staff to access information immediately relevant to Duchenne muscular dystrophy... In order to provide the most up to date clinical information to A&E staff, patients and their carers must make sure their..
Relevance: 18.797562
  • synthena.com
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Synthena AG is a development stage biotechnology company aiming to develop and commercialize new life saving drugs for the treatment of severe neuromuscular diseases based on the modulation of RNA. Its proprietary tricyclo-DNA technology platform..
Relevance: 18.418118
  • charleysfund.org
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He's a neat freak and a fashion maven. He collects sunglasses and watches Chef's Table. He reads restaurant reviews on YELP and loves modern design. He's our founding inspiration for a mission focused on helping everyone with Duchenne. Now 22 years..
Relevance: 18.183155
  • www.zackhegerfoundation.org
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The Zack Heger Foundation is a 501(c)3 charitable foundation started in honor of our son Zack who was diagnosed with a fatal muscle wasting disease, Duchenne Muscular Dystrophy, when he was just 3 years old. Initially, our goal was to fund vital..
Relevance: 18.166733
  • www.jaanbio.com
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Jaan Biotherapeutics, LLC is a private company that is developing novel therapies to activate the cardiac regeneration process in diseased hearts using proprietary technology. The technology manipulates microRNAs to activate an endogenous cardiac..
Relevance: 18.071037
  • teamajsfund.org
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Team AJsFund is a cycling team dedicated to raising awareness about Duchenne muscular dystrophy...
Relevance: 17.768944