Companies similar to RARE DISEASES
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  • www.hse.ie
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The National Rare Diseases Office (NRDO) was established by the HSE in 2015. We are the national rare disease ‘coordination hub' and the HSE main contact and driver of rare disease initiatives and projects. In accordance with the National Rare..
Relevance: 38.74557
  • rarediseasesday.wustl.edu
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According to the National Institutes of Health (NIH), a disease is rare if it affects less than 200,000 people in the United States. Over 25 million Americans live with a rare disease-and nearly half of these patients are children. For the over 7,000..
Relevance: 25.201696
  • travere.com
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Travere Therapeutics is a biopharmaceutical company whose mission is to identify, develop and deliver life-changing therapies to people living with rare disease... SAN DIEGO, Feb. 28, 2022 (GLOBE NEWSWIRE) - Travere Therapeutics, Inc. (NASDAQ: TVTX)..
Relevance: 24.963303
  • irdirc.org
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The International Rare Diseases Research Consortium (IRDiRC) is a global collaborative initiative launched in 2011 by the European Commission and the US National Institutes of Health to tackle rare diseases through research and accomplish the vision..
Relevance: 22.682302
  • geneticdiseases-lab.fr
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During the last years, we have identified a dozen new disease genes and performed several studies combining functional aspects and phenotype:genotype correlations. Our research program can be schematically divided into two main parts: for each..
Relevance: 22.448456
  • www.blackswanfoundation.ch
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Increasing awareness for rare diseases research and therefore improving the understanding of rare diseases among the public, politicians, health professionals, researchers and academics is one of the main objective of the #RAREvolution. BLACKSWAN..
Relevance: 21.540426
  • rdna.ca
The Rare Disease Network of Alberta (rDNA) is a non-profit corporation that was formed in 2018 to help people understand about rare diseases... More than 18,000 Canadians and 2,100 Albertans are expected to have a rare disease and there may be 300..
Relevance: 21.325872
  • www.rareuniversity.com
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RARE University is dedicated to providing trusted and relevant education, training, tools, and resources to make an impact in the Rare disease community... All courses are free and designed with you in mind. From basic to complex, Rare University..
Relevance: 21.09056
  • www.pscpartnersregistry.org
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The PSC Partners Patient Registry: The registry was created with the guidance of the NIH Office of Rare Disease Research (ORDR). In 2012, PSC Partners was one of the rare disease organizations selected by the ORDR to participate in their Global Rare..
Relevance: 20.860157
  • www.engagehealth.com
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Engage Health is a health research and market development firm who has helped companies in the rare disease space for over 25 years... Engage Health's team provides comprehensive services to further development of rare and specialty disease..
Relevance: 20.783552
  • finding-rare.com
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OUr Team Our team's combined 40+ years in the rare disease marketplace and personal experience with the rare disease diagnostic odyssey led us to believe that there had to be a better way. We knew the data to accelerate rare disease diagnoses and..
Relevance: 20.76905
  • connectwithdash.com
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Dash Productions and Event Hosting is an offering from The Dash Alliance for Rare Disease Collaboration, an organization founded in 2015 by rare disease parents and advocates, Eden and Jeff Lord...
Relevance: 20.44136
  • en.sperogenix.com
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Sperogenix Therapeutics is a platform company dedicated to developing and commercializing rare disease therapeutics in China. With prioritized therapeutic areas, such as pulmonary vascular disorders, neuromuscular diseases, and inherited metabolic..
Relevance: 20.424288
  • nationalstemcellfoundation.org
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The National Stem Cell Foundation is a 501(c)3 non-profit organization that funds adult stem cell and regenerative medicine research, connects children with limited resources to clinical trials for rare diseases, and underwrites the National STEM..
Relevance: 20.3787
  • www.erydel.com
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EryDel has formed a team of globally minded, inspired leaders experienced in rare disease drug development and commercialization, highly committed to providing innovative therapies to patients suffering from rare disease conditions...
Relevance: 20.20112
  • www.winhealthgroups.com
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BO'AO WINHEALTH RARE DISEASE MEDICAL CENTER/BO'AO RARE DISEASE MEDICAL CENTER is keeping pace with development of the world to introduce advanced rare disease medical products into Chinese market, bringing new hope to patients with rare disease in..
Relevance: 20.137564
  • ichthyosis.info
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Ichthyosis is considered a rare disease because it appears in 1 in 250.000 births. Currently there is no cure and the treatments are exclusively symptomatic, that is, to calm and reduce damage... The European Network for Ichthyosis, eni, is an..
Relevance: 20.00664
  • www.caspiansafe.com
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Caspian Safe is the first national company in Azerbaijan providing HSE training services for many different companies. Among our major clients are BP and almost all BP contractors... Caspian Safe - a first national HSE Training Provider in the..
Relevance: 19.99926
  • www.cureraredisease.org
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Cure Rare Disease, a non-profit organization (Tax ID number 82-2473513), is qualified as a tax-exempt organization under section 501(c)(3) of the IRS and has been designated as a "public charity" under section 170... Cure Rare Disease™ is developing..
Relevance: 19.972485
  • dudnyk.com
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Dudnyk is a full-service healthcare advertising agency that provides rare insights and creativity, with a rare approach, with rare talent, all within the rare disease space...
Relevance: 19.942553
  • www.swii.ch
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Swii.ch health is a rare disease patient insight agency and strategy consultancy. We help our healthcare clients make better informed decisions based on a deep understanding of human behaviour... In addition to our core team, we work with a wider..
Relevance: 19.89063
  • purposeful.eu
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Purposeful is a biotech company, integrating AI and human expertise to accelerate the development of rare disease treatments... Purposeful discovers new treatments and develops pharmaceutical products for rare diseases, by repurposing already..
Relevance: 19.639332
  • www.rareneuro.com
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Most individuals with a rare disease have never met a specialist in their disorder, and care is inconsistent. Quality of life is often extremely poor, and over 1/3 of deaths in early childhood are due to a rare disease. At the Center for Rare..
Relevance: 19.63867
  • eusapharma.com
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Eusa Pharma is part of Recordati Rare Diseases, the business unit dedicated to rare disease in the Recordati group. Recordati has a total staff of more than 4,300, dedicated to the research, development, manufacturing and marketing of..
Relevance: 19.524956
  • www.tmaprecisionhealth.com
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TMA is built by rare disease families for this exact purpose: to give patients and their care teams a genetic diagnosis, more disease information, and personalized treatment options... Our mission is to improve the lives of rare disease patients,..
Relevance: 19.509985
  • laldsource.com
LAL-D is a rare, genetic disease that causes enzyme deficiency leading to progressive and ongoing multiorgan damage. 2... Lysosomal Acid Lipase Deficiency (LAL-D) is a rare, genetic disease that causes progressive and ongoing damage...
Relevance: 19.451239
  • www.actionduchenne.org
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Hope and Determination on Rare Disease Day 2024 Today, 29th February 2024, marks Rare Disease Day. At Action Duchenne, we join with the global rare disease community to shine a light on the 300 million people across the world living with rare..
Relevance: 19.429394
  • casimirtrials.com
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The new approach to rare disease research. Through new-age clinical trials, Casimir is leading the way to better understand disease progression and treatment... At Casimir, we combine our knowledge of living with rare disease with our experience in..
Relevance: 19.416582
  • www.squarerootthinking.com
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Square Root is a healthcare consultancy based in Europe. We celebrate the variation in clinical practice, as the hotbed of new emerging best practice and innovation. Adopting simple outcomes as the common currency to codify knowledge and..
Relevance: 19.39686
  • www.stampoutoncho.org
Onchocerciasis (river blindness) elimination is at risk of losing momentum now that the disease is under control as "a public health problem." In most endemic areas, blindness is increasingly rare and skin disease is not as prevalent as it once was..
Relevance: 19.376364