BIOMARIN

NCT07126262 A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months Trial Status Recruiting NCT06212947 A Multicenter Multinational Observational Study of Children With Hypochondroplasia Trial Status Recruiting NCT06280209 A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy Trial Status Recruiting NCT06738017 Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants Trial Status Recruiting NCT06309979 A Study to Assess Growth in Children With Idiopathic Short Stature Trial Status Recruiting NCT06382155 A Phase 2 Study of Vosoritide in Children with Idiopathic Short Stature Trial Status Recruiting NCT06668805 A Phase 2 Basket Study of Vosoritide in Children With Turner Syndrome, SHOX Deficiency and Noonan Syndrome With an Inadequate Response to Human Growth Hormone Trial Status Recruiting NCT04404530 Nutritional Impacts of Palynziq on..

Also known as: BioMarin Clinical Trials, BioMarin Pharmaceutical Inc.