MITOCHONDRIAL DISEASE NEWS

Niacin, vitamin B3, can help to normalize muscle metabolism in people with mitochondrial myopathy, a study based on a small pilot trial in patients suggests. Titled, "Niacin Cures Systemic NAD+ Deficiency and Improves Muscle Performance in Adult-Onset Mitochondrial Myopathy," the study was published in the…... An independent Data Safety Monitoring Board (DSMB) has found GS030, GenSight Biologics' candidate gene therapy for retinitis pigmentosa, safe and recommended the company's PIONEER trial continue as planned. PIONEER (NCT03326336) is a Phase 1/2 trial currently investigating the safety and tolerability of increasing doses of GS030…

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