URGENT RESEARCH

This page tracks new and upcoming treatment options for Batten disease. What's in development? What's promising? What's available soon? Current topics include BBDF-101, gene therapy, AT-GTX-502, AT-GTX-501, AAV2CUhCLN2, BMN 190, Brineura (cerliponase alfa), AB-202, AB-201, and more. Jump to section: News, Research, Clinical Trials, Projects

Also known as: Batten Treatment Report